Feb 16, 2024
Joe Scalia, Vice President and Head of Commercial Market Access and Global Marketing for Mitsubishi Tanabe Pharma America, highlights the company's focus on rare diseases, particularly ALS, amyotrophic lateral sclerosis, also known as Lou Gehrig's disease. The company's goal is to find a cure for ALS and improve...
Feb 16, 2024
Joe Scalia, Vice President and Head of Commercial Market Access and Global Marketing for Mitsubishi Tanabe Pharma America, highlights the company's focus on rare diseases, particularly ALS, amyotrophic lateral sclerosis, also known as Lou Gehrig's disease. The company's goal is to find a cure for ALS and improve...
Nov 7, 2023
Brian Strem, President and CEO of Kiora Pharmaceuticals, is developing a small molecule drug to treat orphan retinal diseases. Their drug KIO-301 restores vision in patients with inherited retinal disease. By giving retinal ganglion cells the ability to sense light, signals can be sent to the brain to effectively see...
Nov 7, 2023
Brian Strem, President and CEO of Kiora Pharmaceuticals, is developing a small molecule drug to treat orphan retinal diseases. Their drug KIO-301 restores vision in patients with inherited retinal disease. By giving retinal ganglion cells the ability to sense light, signals can be sent to the brain to effectively see...
Aug 21, 2023
Dr. Björn Mellgård, VP and Global Program Lead of rare genetics and hematology at Takeda, is passionate about finding a cure for cTTP, congenital thrombotic thrombocytopenic purpura. This ultra-rare disease, caused by an enzyme deficiency, presents in early childhood and results in life-threatening blood clots....